Recent Posts

• Audentes Therapeutics’ “Be Bold for Courageous Patients” Program to Support Patients Living with Rare Diseases
• Amicus Therapeutics establishes a 75,000 sq. ft. Gene Therapy Center of Excellence
• Amicus Therapeutics Receives Breakthrough Therapy Designation for Pompe Treatment
• Rare Disease Day 2019
• Sarepta Therapeutics Enters into a Strategic Relationship with Aldevron in Support of Their Gene Therapy Program