Dealing with disability or in my case multiple disabilities opens you up to a different perspective about life. I believe that this has helped shape me as a better person. I’d like to share these lessons and insights with you.
- Sarepta Therapeutics Enters into a Strategic Relationship with Aldevron in Support of Their Gene Therapy Program
- CAP Walks for Muscular Dystrophy in 2018
- Amicus Therapeutics Announces First Patient Dosed in Phase 3 PROPEL Study of AT-GAA in Patients with Pompe Disease
- Audentes Therapeutics Pompe Program Update
- Amicus Therapeutics Enters Research and Development Collaboration with University of Pennsylvania to Develop AAV Gene Therapies