Dealing with disability or in my case multiple disabilities opens you up to a different perspective about life. I believe that this has helped shape me as a better person. I’d like to share these lessons and insights with you.
- Audentes Therapeutics Pompe Program Update
- Amicus Therapeutics Enters Research and Development Collaboration with University of Pennsylvania to Develop AAV Gene Therapies
- Spark Therapeutics Announces New Preclinical Data for Their Pompe Disease Gene Therapy Candidate
- Amicus Therapeutics Announces Positive 18-Month Data in Pompe Disease Phase 1/2 Study
- Audentes Therapeutics program update for Pompe disease