John F. Crowley
John Crowley, Chairman of the Board and CEO of Amicus Therapeutics, discussing family, challenges when entering adulthood, newborn screening and what’s new at Amicus.
Cheryl Wong Po Foo
Cheryl Wong Po Foo, PhD, Director of Clinical Development, Astellas Gene Therapies, responsible for the advancement of the clinical development program for Pompe disease.
Naresh Kumar Meena and Nina Raben
Leading researchers from the NIH discuss the discovery of Pompe disease, Pompe disease research studies at the NIH, and the recognition of a new phenotype for Pompe disease following the introduction of enzyme replacement therapy.