An eLearning module to learn about Pompe Disease, by going through the journey of Sam, recently diagnosed with Pompe Disease.
- Audentes Therapeutics Pompe Program Update
- Amicus Therapeutics Enters Research and Development Collaboration with University of Pennsylvania to Develop AAV Gene Therapies
- Spark Therapeutics Announces New Preclinical Data for Their Pompe Disease Gene Therapy Candidate
- Amicus Therapeutics Announces Positive 18-Month Data in Pompe Disease Phase 1/2 Study
- Audentes Therapeutics program update for Pompe disease